Your donation supports cutting-edge research, including promising approaches like tRNA therapy, to treat — and potentially cure — Duchenne Muscular Dystrophy (DMD). Our focus is on nonsense mutations, which not only affect those with DMD but are linked to many rare diseases impacting over 3 million people in the U.S. alone.

By contributing, you're advancing science that could help countless families facing rare genetic disorders. Every dollar brings us closer to breakthrough treatments — and fuels the resolve to find a cure.